Paradigm shift in SMA

Videos:

Eugenio Mercuri, Professor of Paediatric Neurology and Head of the Paediatric Neurology and Psychiatry Unit of the Gemelli Hospital Catholic University Foundation, Rome, Italy, is talking about the the importance of RWE in SMA (rare diseases) and the importance of registries.

Video Interview Prof. Dr. Hagenacker "New Data on the Treatment of adult SMA with NUS"

Video Interview Prof. Dr. Kleinschnitz "Treatment of SMA in adult patients"

Agneta Markstrom presentation

Zac's play day

Marika Pane interview

Thomas Sejersen interview

Agneta Markstrom interview

Mar Tulinius interview

A critical review and meta-analysis